
Professor of Clinical Pediatrics
Chief, Division of Pediatric Allergy, Immunology & Bone Marrow Transplantation; Medical Director, Pediatric Cellular Therapy Laboratory, UCSF Benioff Children's Hospital
M_PEDS-AIBMT-CORE-BONE MAR TRA
+1 415 476-2188
My Research Interests are divided into 3 areas of focus:
1. Supportive Care (especially Invasive Fungal Infections) following Hematopoietic Stem Cell Transplantation
2. Transplantation for Severe Combined Immunodeficiency
3. Transplantation for Rare Leukemias (JMML and APL)
Publications
A Randomized Clinical Trial Evaluating Lactiplantibacillus Plantarum for the Prevention of GI aGvHD: A Report From the Children's Oncology Group (ACCL1633).
Transplantation and cellular therapy
High Melphalan Exposure Increases the Risk of Graft-versus-Host Disease in Pediatric Patients Undergoing Alpha-Beta T-Cell Depleted Haploidentical Transplantation.
Transplantation and cellular therapy
Integrating Pulmonary and Systemic Transcriptomic Profiles to Characterize Lung Injury after Pediatric Hematopoietic Stem Cell Transplant.
medRxiv : the preprint server for health sciences
Younger Children with Non-Malignant Disease Have Increased Incidence of Mixed Myeloid Chimerism After Allogeneic Hematopoietic Cell Transplantation with Busulfan-Based Conditioning.
Transplantation and cellular therapy
Prevention and Management of Infectious Complications in Pediatric Patients With Cancer: A Survey Assessment of Current Practices Across Children's Oncology Group Institutions.
Pediatric blood & cancer
Effect of Rabbit ATG PK on Outcomes after TCR-αβ/CD19-depleted Pediatric Haploidentical HCT for Hematologic Malignancy.
Blood advances
Hematopoietic Stem Cell Transplantation for C1q Deficiency: A Study on Behalf of the EBMT Inborn Errors Working Party.
Journal of clinical immunology
Association of Busulfan Exposure and Outcomes after HCT for Patients with an Inborn Error of Immunity.
Blood advances
High symptom burden in female X-linked chronic granulomatous disease carriers.
Clinical immunology (Orlando, Fla.)
Epidemiology of Diffuse Alveolar Hemorrhage in Pediatric Allogeneic Hematopoietic Cell Transplant Recipients.
Transplantation and cellular therapy
Cyclophosphamide and thiotepa increases risk of transplant-associated thrombotic microangiopathy.
Transplantation and cellular therapy
Pulmonary hypertension in the intensive care unit after pediatric allogeneic hematopoietic stem cell transplant: incidence, risk factors, and outcomes.
Frontiers in oncology
Pathobiological signatures of dysbiotic lung injury in pediatric patients undergoing stem cell transplantation.
Nature medicine
Diagnosing and Grading of Sinusoidal Obstructive Syndrome after Hematopoietic Stem Cell Transplant of Children, Adolescent and Young Adults treated in a Pediatric Institution with Pediatric Protocols.
Transplantation and cellular therapy
Intensive Care Risk and Long-Term Outcomes in Pediatric Allogeneic Hematopoietic Cell Transplant Recipients.
Blood advances
Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia.
Clinical immunology (Orlando, Fla.)
Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: a PIDTC study.
The Journal of allergy and clinical immunology
Pulmonary microbiome and transcriptome signatures reveal distinct pathobiologic states associated with mortality in two cohorts of pediatric stem cell transplant patients.
medRxiv : the preprint server for health sciences
Post-Transplant Late Complications Increase Over Time for Patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) Landmark Study.
The Journal of allergy and clinical immunology
No impact of CD34+ cell dose on outcome among children undergoing autologous hematopoietic stem cell transplant for high-risk neuroblastoma.
Bone marrow transplantation
Intestinal microbiome and metabolome signatures in patients with chronic granulomatous disease.
The Journal of allergy and clinical immunology
Critical Illness Risk and Long-Term Outcomes Following Intensive Care in Pediatric Hematopoietic Cell Transplant Recipients.
medRxiv : the preprint server for health sciences
Diffuse alveolar hemorrhage after hematopoietic cell transplantation- response to treatments and risk factors for mortality.
Frontiers in oncology
Children's Oncology Group's 2023 blueprint for research: Cancer control and supportive care.
Pediatric blood & cancer
Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium.
Lancet (London, England)
What causes aplastic anaemia?
Leukemia
Effect of Autograft CD34+ Dose on Outcome in Pediatric Patients Undergoing Autologous Hematopoietic Stem Cell Transplant for Central Nervous System Tumors.
Transplantation and cellular therapy
Fertility Preservation Practices at Pediatric Oncology Institutions in the United States: A Report From the Children's Oncology Group.
JCO oncology practice
What Causes Aplastic Anaemia: Results of Transplants from Genetically-Identical Twins.
Research square
Lentiviral Gene Therapy for Artemis-Deficient SCID.
The New England journal of medicine
Impact of Genetic Diagnosis on the Outcome of Hematopoietic Stem Cell Transplant in Primary Immunodeficiency Disorders.
Journal of clinical immunology
The diagnosis of severe combined immunodeficiency (SCID): The Primary Immune Deficiency Treatment Consortium (PIDTC) 2022 Definitions.
The Journal of allergy and clinical immunology
The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions.
The Journal of allergy and clinical immunology
Prospective Evaluation of the Fungitell� (1?3) Beta-D-Glucan Assay as a Diagnostic Tool for Invasive Fungal Disease in Pediatric Allogeneic Hematopoietic Cell Transplantation: A�Report from the Children's Oncology Group.
Pediatric transplantation
Aberrant T-cell exhaustion in severe combined immunodeficiency survivors with poor T-cell reconstitution after transplantation.
The Journal of allergy and clinical immunology
A Population-Based Study of the Long-Term Risk of Infections Associated With Hospitalization in Childhood Cancer Survivors.
Journal of clinical oncology : official journal of the American Society of Clinical Oncology
Granulocyte Transfusions in Patients with Chronic Granulomatous Disease Undergoing Hematopoietic Cell Transplantation or Gene Therapy.
Journal of clinical immunology
Challenges and Barriers to Adverse Event Reporting in Clinical Trials: A Children's Oncology Group Report.
Journal of patient safety
Population Pharmacokinetics of Melphalan for Pediatric Patients Undergoing Hematopoietic Cell Transplantation.
Journal of clinical pharmacology
Pulmonary microbiome and gene expression signatures differentiate lung function in pediatric hematopoietic cell transplant candidates.
Science translational medicine
A pilot trial of prophylactic defibrotide to prevent serious thrombotic microangiopathy in high-risk pediatric patients.
Pediatric blood & cancer
Association Between the Magnitude of Intravenous Busulfan Exposure and Development of Hepatic Veno-Occlusive Disease in Children and Young Adults Undergoing Myeloablative Allogeneic Hematopoietic Cell Transplantation.
Transplantation and cellular therapy
Therapy-related myeloid neoplasms resembling juvenile myelomonocytic leukemia: a case series and review of the literature.
Pediatric blood & cancer
Population Pharmacokinetic Model Development of Tacrolimus in Pediatric and Young Adult Patients Undergoing Hematopoietic Cell Transplantation.
Frontiers in pharmacology
Hematopoietic Cell Transplantation-Comorbidity Index Score Is Correlated with Treatment-Related Mortality and Overall Survival following Second Allogeneic Hematopoietic Cell Transplantation in Children.
Transplantation and cellular therapy
Juvenile myelomonocytic leukemia in the molecular era: a clinician's guide to diagnosis, risk stratification, and treatment.
Blood advances
The Beginning of the End of Allogeneic Transplantation for Hurler Syndrome?
The New England journal of medicine
Infrastructure of Fertility Preservation Services for Pediatric Cancer Patients: A Report From the Children's Oncology Group.
JCO oncology practice
Prospective Evaluation of Galactomannan and (1→3) β-d-Glucan Assays as Diagnostic Tools for Invasive Fungal Disease in Children, Adolescents, and Young Adults With Acute Myeloid Leukemia Receiving Fungal Prophylaxis.
Journal of the Pediatric Infectious Diseases Society
Poor T-cell receptor β repertoire diversity early posttransplant for severe combined immunodeficiency predicts failure of immune reconstitution.
The Journal of allergy and clinical immunology
Comparison of hematopoietic cell transplant conditioning regimens for hemophagocytic lymphohistiocytosis disorders.
The Journal of allergy and clinical immunology
NUP98-NSD1 Driven MDS/MPN in Childhood Masquerading as JMML.
Journal of pediatric hematology/oncology
A Guidance for Concomitant Drug Reconciliation Prior to Allogeneic Hematopoietic Cell Transplantation in Children and Young Adults.
Frontiers in pediatrics
International retrospective study of allogeneic hematopoietic cell transplantation for activated PI3K-delta syndrome.
The Journal of allergy and clinical immunology
A Randomized Trial of Caspofungin vs Triazoles Prophylaxis for Invasive Fungal Disease in Pediatric Allogeneic Hematopoietic Cell Transplant.
Journal of the Pediatric Infectious Diseases Society
Transplant-associated thrombotic microangiopathy in pediatric patients: pre-HSCT risk stratification and prophylaxis.
Blood advances
Musculoskeletal impairments in children receiving intensive therapy for acute leukemia or undergoing hematopoietic stem cell transplant: A report from the Children's Oncology Group.
Pediatric blood & cancer
Vitamin D has no impact on outcomes after HSCT in children-A retrospective study.
Pediatric transplantation
Correction to: Infections in Infants with SCID: Isolation, Infection Screening and Prophylaxis in PIDTC Centers.
Journal of clinical immunology
A pragmatic multi-institutional approach to understanding transplant-associated thrombotic microangiopathy after stem cell transplant.
Blood advances
The Relationship Between Busulfan Exposure and Achievement of Sustained Donor Myeloid Chimerism in Patients with Non-Malignant Disorders.
Transplantation and cellular therapy
Unknown cytomegalovirus serostatus in primary immunodeficiency disorders: A new category of transplant recipients.
Transplant infectious disease : an official journal of the Transplantation Society
Correction: Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT.
Journal of clinical immunology
Infections in Infants with SCID: Isolation, Infection Screening, and Prophylaxis in PIDTC Centers.
Journal of clinical immunology
How We Treat Fever and Hypotension in Pediatric Hematopoietic Cell Transplant Patients.
Frontiers in oncology
Assessment of provider perspectives on otoprotection research for children and adolescents: A Children's Oncology Group Cancer Control and Supportive Care Committee survey.
Pediatric blood & cancer
Lower Exposure to Busulfan Allows for Stable Engraftment of Donor Hematopoietic Stem Cells in Children with Mucopolysaccharidosis Type I: A Case Report of Four Patients.
International journal of molecular sciences
Assessment of a Model-Informed Precision Dosing Platform Use in Routine Clinical Care for Personalized Busulfan Therapy in the Pediatric Hematopoietic Cell Transplantation (HCT) Population.
Frontiers in pharmacology
Reduced Toxicity Conditioning for Nonmalignant Hematopoietic Cell Transplants.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Practice patterns and incidence of adenovirus infection in allogeneic hematopoietic cell transplant recipients: Multicenter survey of transplant centers in the United States.
Transplant infectious disease : an official journal of the Transplantation Society
Hematopoietic Cell Transplantation in Patients With Primary Immune Regulatory Disorders (PIRD): A Primary Immune Deficiency Treatment Consortium (PIDTC) Survey.
Frontiers in immunology
TA-TMA: state of the art for diagnosis and treatment.
Blood advances
Extended Follow-up After Hematopoietic Cell Transplantation for IκBα Deficiency with Disseminated Mycobacterium avium Infection.
Journal of clinical immunology
The impact of total body irradiation-based regimens on outcomes in children and young adults with acute lymphoblastic leukemia undergoing allogeneic hematopoietic stem cell transplantation.
Pediatric blood & cancer
Choice of conditioning regimens for bone marrow transplantation in severe aplastic anemia.
Blood advances
Comprehensive Prognostication in Critically Ill Pediatric Hematopoietic Cell Transplant Patients: Results from Merging the Center for International Blood and Marrow Transplant Research (CIBMTR) and Virtual Pediatric Systems (VPS) Registries.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Related and unrelated donor transplantation for β-thalassemia major: results of an international survey.
Blood advances
Acupressure to Reduce Treatment-Related Symptoms for Children With Cancer and Recipients of Hematopoietic Stem Cell Transplant: Protocol for a Randomized Controlled Trial.
Global advances in health and medicine
Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT.
Journal of clinical immunology
Molecular assessment of pretransplant chemotherapy in the treatment of juvenile myelomonocytic leukemia.
Pediatric blood & cancer
Risk Factors for Transplant-Associated Thrombotic Microangiopathy after Autologous Hematopoietic Cell Transplant in High-Risk Neuroblastoma.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Pulmonary Metagenomic Sequencing Suggests Missed Infections in Immunocompromised Children.
Clinical infectious diseases : an official publication of the Infectious Diseases Society of America
Autoimmune Cytopenias in Pediatric Hematopoietic Cell Transplant Patients.
Frontiers in pediatrics
Population Pharmacokinetics of Clofarabine as Part of Pretransplantation Conditioning in Pediatric Subjects before Hematopoietic Cell Transplantation.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Transplant-Associated Thrombotic Microangiopathy in Pediatric Hematopoietic Cell Transplant Recipients: A Practical Approach to Diagnosis and Management.
Frontiers in pediatrics
Low Exposure Busulfan Conditioning to Achieve Sufficient Multilineage Chimerism in Patients with Severe Combined Immunodeficiency.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Determination of melphalan in human plasma by UPLC-UV method.
Cancer chemotherapy and pharmacology
Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study.
The Journal of allergy and clinical immunology
Early Plasma Matrix Metalloproteinase Profiles. A Novel Pathway in Pediatric Acute Respiratory Distress Syndrome.
American journal of respiratory and critical care medicine
Higher Risks of Toxicity and Incomplete Recovery in 13- to 17-Year-Old Females after Marrow Donation: RDSafe Peds Results.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Bacterial blood stream infections (BSIs), particularly post-engraftment BSIs, are associated with increased mortality after allogeneic hematopoietic cell transplantation.
Bone marrow transplantation
Effect of Aging and Predonation Comorbidities on the Related Peripheral Blood Stem Cell Donor Experience: Report from the Related Donor Safety Study.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Daratumumab in life-threatening autoimmune hemolytic anemia following hematopoietic stem cell transplantation.
Blood advances
Identifying clinical practice guidelines for the supportive care of children with cancer: A report from the Children's Oncology Group.
Pediatric blood & cancer
Outcomes after Second Hematopoietic Cell Transplantation in Children and Young Adults with Relapsed Acute Leukemia.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Comment on: Olanzapine for chemotherapy-induced nausea: Lessons learned from child and adolescent psychiatry.
Pediatric blood & cancer
The genetic landscape of severe combined immunodeficiency in the United States and Canada in the current era (2010-2018).
The Journal of allergy and clinical immunology
Veno-occlusive disease after high-dose busulfan-melphalan in neuroblastoma.
Bone marrow transplantation
Practice pattern changes and improvements in hematopoietic cell transplantation for primary immunodeficiencies.
The Journal of allergy and clinical immunology
Chronic norovirus infection in primary immune deficiency disorders: an international case series.
Diagnostic microbiology and infectious disease
Outcome of domino hematopoietic stem cell transplantation in human subjects: An international case series.
The Journal of allergy and clinical immunology
Outcomes of Measurable Residual Disease in Pediatric Acute Myeloid Leukemia before and after Hematopoietic Stem Cell Transplant: Validation of Difference from Normal Flow Cytometry with Chimerism Studies and Wilms Tumor 1 Gene Expression.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Comparison of pediatric allogeneic transplant outcomes using myeloablative busulfan with cyclophosphamide or fludarabine.
Blood advances
Late cardiovascular morbidity and mortality following pediatric allogeneic hematopoietic cell transplantation.
Bone marrow transplantation
Disease burden and conditioning regimens in ASCT1221, a randomized phase II trial in children with juvenile myelomonocytic leukemia: A Children's Oncology Group study.
Pediatric blood & cancer
Metagenomic Sequencing Detects Respiratory Pathogens in Hematopoietic Cellular Transplant Patients.
American journal of respiratory and critical care medicine
Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study.
The Journal of allergy and clinical immunology
Pediatric Hematopoietic Cell Transplant Patients Who Survive Critical Illness Frequently Have Significant but Recoverable Decline in Functional Status.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Pulmonary veno-occlusive disease in a pediatric hematopoietic stem cell transplant patient: a cautionary tale.
Leukemia & lymphoma
Neurologic event-free survival demonstrates a benefit for SCID patients diagnosed by newborn screening.
Blood advances
Consensus Report by the Pediatric Acute Lung Injury and Sepsis Investigators and Pediatric Blood and Marrow Transplantation Consortium Joint Working Committees on Supportive Care Guidelines for Management of Veno-Occlusive Disease in Children and Adolesce
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Consensus Report by the Pediatric Acute Lung Injury and Sepsis Investigators and Pediatric Blood and Marrow Transplant Consortium Joint Working Committees on Supportive Care Guidelines for Management of Veno-Occlusive Disease in Children and Adolescents:
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Reducing Second Gram-Negative Antibiotic Therapy on Pediatric Oncology and Hematopoietic Stem Cell Transplantation Services.
Infection control and hospital epidemiology
Opening Marrow Niches in Patients Undergoing Autologous Hematopoietic Stem Cell Gene Therapy.
Hematology/oncology clinics of North America
Consensus Report by Pediatric Acute Lung Injury and Sepsis Investigators and Pediatric Blood and Marrow Transplantation Consortium Joint Working Committees: Supportive Care Guidelines for Management of Veno-Occlusive Disease in Children and Adolescents, P
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Pharmacokinetics and Model-Based Dosing to Optimize Fludarabine Therapy in Pediatric Hematopoietic Cell Transplant Recipients.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Burden of illness associated with sinusoidal obstruction syndrome/veno-occlusive disease in patients with hematopoietic stem cell transplantation.
Journal of medical economics
Extracorporeal life support survival in a pediatric hematopoietic cellular transplant recipient with presumed GvHD-related fulminant myocarditis.
Bone marrow transplantation
Unconditioned unrelated donor bone marrow transplantation for IL7Rα- and Artemis-deficient SCID.
Bone marrow transplantation
Safety of pre-emptive donor lymphocyte infusions (DLI) based on mixed chimerism (MC) in peripheral blood or bone marrow subsets in children undergoing hematopoietic stem cell transplant (HSCT) for hematologic malignancies.
Bone marrow transplantation
Eosinophilic Pustular Folliculitis in Children after Stem Cell Transplantation: An Eruption Distinct from Graft-Versus-Host Disease.
Pediatric dermatology
Treatment of infants identified as having severe combined immunodeficiency by means of newborn screening.
The Journal of allergy and clinical immunology
Early mixed chimerism-based preemptive immunotherapy in children undergoing allogeneic hematopoietic stem cell transplantation for acute leukemia.
Pediatric blood & cancer
A Multicenter Study of Bacterial Blood Stream Infections in Pediatric Allogeneic Hematopoietic Cell Transplantation Recipients: The Role of Acute Gastrointestinal Graft-versus-Host Disease.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Pre-existing invasive fungal infection is not a contraindication for allogeneic HSCT for patients with hematologic malignancies: a CIBMTR study.
Bone marrow transplantation
Hematopoietic stem cell transplant in patients with activated PI3K delta syndrome.
The Journal of allergy and clinical immunology
Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis.
The Lancet. Haematology
Long-term outcomes of 176 patients with X-linked hyper-IgM syndrome treated with or without hematopoietic cell transplantation.
The Journal of allergy and clinical immunology
Evaluation of Pre-Hematopoietic Cell Transplantation (HCT) Brain MRI and Neurologic Complications of Pediatric Patients Undergoing HCT for Hematologic Malignancies.
Journal of pediatric oncology nursing : official journal of the Association of Pediatric Oncology Nurses
Severe, persistent, and fatal T-cell immunodeficiency following therapy for infantile leukemia.
Pediatric blood & cancer
Transplacental maternal engraftment and posttransplantation graft-versus-host disease in children with severe combined immunodeficiency.
The Journal of allergy and clinical immunology
Risk of serious bloodstream infections is low in pediatric hematopoietic stem cell transplant (HSCT) recipients with fevers due to antithymocyte globulins and alemtuzumab.
Bone marrow transplantation
Safe and Effective Prophylaxis with Bimonthly Intravenous Pentamidine in the Pediatric Hematopoietic Stem Cell Transplant Population.
The Pediatric infectious disease journal
The incidence, mortality and timing of Pneumocystis jiroveci pneumonia after hematopoietic cell transplantation: a CIBMTR analysis.
Bone marrow transplantation
Plasma angiopoietin-2 outperforms other markers of endothelial injury in prognosticating pediatric ARDS mortality.
American journal of physiology. Lung cellular and molecular physiology
Classification of treatment-related mortality in children with cancer: a systematic assessment.
The Lancet. Oncology
New Insights Into Multicenter PICU Mortality Among Pediatric Hematopoietic Stem Cell Transplant Patients.
Critical care medicine
Transplant Outcomes for Children with T Cell Acute Lymphoblastic Leukemia in Second Remission: A Report from the Center for International Blood and Marrow Transplant Research.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Transplantation Outcomes for Children with Hypodiploid Acute Lymphoblastic Leukemia.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Population pharmacokinetics of busulfan in pediatric and young adult patients undergoing hematopoietic cell transplant: a model-based dosing algorithm for personalized therapy and implementation into routine clinical use.
Therapeutic drug monitoring
The Sequence of Cyclophosphamide and Myeloablative Total Body Irradiation in Hematopoietic Cell Transplantation for Patients with Acute Leukemia.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Hematopoietic Stem Cell Transplantation for Severe Combined Immunodeficiency.
Current pediatrics reports
Repeat blood cultures in children with persistent fever and neutropenia: Diagnostic and clinical implications.
Pediatric blood & cancer
Juvenile myelomonocytic leukemia.
Pediatric clinics of North America
Chimerism-based pre-emptive immunotherapy with fast withdrawal of immunosuppression and donor lymphocyte infusions after allogeneic stem cell transplantation for pediatric hematologic malignancies.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia.
Haematologica
TNF-receptor inhibitor therapy for the treatment of children with idiopathic pneumonia syndrome. A joint Pediatric Blood and Marrow Transplant Consortium and Children's Oncology Group Study (ASCT0521).
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Comparison of outcomes of hematopoietic stem cell transplantation without chemotherapy conditioning by using matched sibling and unrelated donors for treatment of severe combined immunodeficiency.
The Journal of allergy and clinical immunology
Transplantation outcomes for severe combined immunodeficiency, 2000-2009.
The New England journal of medicine
A Prospective, International Cohort Study of Invasive Mold Infections in Children.
Journal of the Pediatric Infectious Diseases Society
Outcomes after hematopoietic stem cell transplantation for children with I-cell disease.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Treatment of hepatoblastoma with high-dose chemotherapy and stem cell rescue: the pediatric blood and marrow transplant consortium experience and review of the literature.
Journal of pediatric hematology/oncology
A trial of alemtuzumab adjunctive therapy in allogeneic hematopoietic cell transplantation with minimal conditioning for severe combined immunodeficiency.
Pediatric transplantation
A trial of plerixafor adjunctive therapy in allogeneic hematopoietic cell transplantation with minimal conditioning for severe combined immunodeficiency.
Pediatric transplantation
Simultaneous determination of fludarabine and clofarabine in human plasma by LC-MS/MS.
Journal of chromatography. B, Analytical technologies in the biomedical and life sciences
Juvenile myelomonocytic leukemia: molecular pathogenesis informs current approaches to therapy and hematopoietic cell transplantation.
Frontiers in pediatrics
Establishing diagnostic criteria for severe combined immunodeficiency disease (SCID), leaky SCID, and Omenn syndrome: the Primary Immune Deficiency Treatment Consortium experience.
The Journal of allergy and clinical immunology
Primary Immune Deficiency Treatment Consortium (PIDTC) report.
The Journal of allergy and clinical immunology
Effect of weight and maturation on busulfan clearance in infants and small children undergoing hematopoietic cell transplantation.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
The natural history of children with severe combined immunodeficiency: baseline features of the first fifty patients of the primary immune deficiency treatment consortium prospective study 6901.
Journal of clinical immunology
Children's Oncology Group's 2013 blueprint for research: stem cell transplantation.
Pediatric blood & cancer
Results from a prospective, international, epidemiologic study of invasive candidiasis in children and neonates.
The Pediatric infectious disease journal
Haploidentical related-donor hematopoietic cell transplantation in children using megadoses of CliniMACs-selected CD34(+) cells and a fixed CD3(+) dose.
Bone marrow transplantation
Clinical outcome in IL-10- and IL-10 receptor-deficient patients with or without hematopoietic stem cell transplantation.
The Journal of allergy and clinical immunology
Busulfan, fludarabine, and alemtuzumab as a reduced toxicity regimen for children with malignant and nonmalignant diseases improves engraftment and graft-versus-host disease without delaying immune reconstitution.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Massage for children undergoing hematopoietic cell transplantation: a qualitative report.
Evidence-based complementary and alternative medicine : eCAM
Hematopoietic cell transplant and use of massage for improved symptom management: results from a pilot randomized control trial.
Evidence-based complementary and alternative medicine : eCAM
National Cancer Institute, National Heart, Lung and Blood Institute/Pediatric Blood and Marrow Transplantation Consortium First International Consensus Conference on late effects after pediatric hematopoietic cell transplantation: the need for pediatric-s
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Complications of transplant for nonmalignant disorders: autoimmune cytopenias, opportunistic infections, and PTLD.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Antifungal prophylaxis in pediatric hematology/oncology: new choices & new data.
Pediatric blood & cancer
Epidemiology and potential preventative measures for viral infections in children with malignancy and those undergoing hematopoietic cell transplantation.
Pediatric blood & cancer
Prevention of bacterial infection in pediatric oncology: what do we know, what can we learn?
Pediatric blood & cancer
NCI, NHLBI/PBMTC first international conference on late effects after pediatric hematopoietic cell transplantation: endocrine challenges-thyroid dysfunction, growth impairment, bone health, & reproductive risks.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
NCI, NHLBI first international consensus conference on late effects after pediatric hematopoietic cell transplantation: state of the science, future directions.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Outcome of myeloablative conditioning and unrelated donor hematopoietic cell transplantation for childhood acute lymphoblastic leukemia in third remission.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Short tandem repeat and human leukocyte antigen mutations or losses confound engraftment and typing analysis in hematopoietic stem cell transplants.
Human immunology
Severe neonatal congenital erythropoietic porphyria.
Pediatric dermatology
Safety of the live, attenuated varicella vaccine in pediatric recipients of hematopoietic SCTs.
Bone marrow transplantation
Radiosensitive severe combined immunodeficiency disease.
Immunology and allergy clinics of North America
The tortoise and the hare: slow and steady stem cells win the race.
Leukemia research
Development of herpes simplex virus stomatitis during receipt of cidofovir therapy.
Clinical infectious diseases : an official publication of the Infectious Diseases Society of America
Clinical and immunologic outcomes following haplocompatible donor lymphocyte infusions.
Bone marrow transplantation
Primary graft failure after umbilical cord blood transplant rescued by parental haplocompatible stem cell transplantation.
Journal of pediatric hematology/oncology
Pathological evidence of Wolman's disease following hematopoietic stem cell transplantation despite correction of lysosomal acid lipase activity.
Bone marrow transplantation
Safety of hematopoietic stem cell transplantation in children less than three years of age.
Pediatric hematology and oncology
High-dose chemotherapy followed by stem cell rescue for high-risk germ cell tumors: the Stanford experience.
Bone marrow transplantation
Megadose CD34(+) cell grafts improve recovery of T cell engraftment but not B cell immunity in patients with severe combined immunodeficiency disease undergoing haplocompatible nonmyeloablative transplantation.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Hematopoietic stem cell transplant for pediatric acute promyelocytic leukemia.
Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Maternal T-cell engraftment associated with severe hemophagocytosis of the bone marrow in untreated X-linked severe combined immunodeficiency.
Journal of pediatric hematology/oncology
Pediatric invasive aspergillosis: a multicenter retrospective analysis of 139 contemporary cases.
Pediatrics
Increasing mixed chimerism and the risk of graft loss in children undergoing allogeneic hematopoietic stem cell transplantation for non-malignant disorders.
Bone marrow transplantation
Liposomal amphotericin B associated with severe hyperphosphatemia.
The Pediatric infectious disease journal
Hematopoietic stem cell transplantation for primary immunodeficiency disease.
Bone marrow transplantation
Reinduction of relapsed acute promyelocytic leukemia with ATRA and low dose antimetabolite-based chemotherapy.
Pediatric blood & cancer
Optimizing care for GI disorders in children after hematopoietic stem cell transplantation.
Gastrointestinal endoscopy
Use of intravenous mycophenolate mofetil for graft-versus-host disease prophylaxis in an allogeneic hematopoietic stem cell transplant recipient with an allergic reaction to cyclosporine and tacrolimus.
Bone marrow transplantation
Risks and outcomes of invasive fungal infections in pediatric patients undergoing allogeneic hematopoietic cell transplantation.
Bone marrow transplantation
Hospital resource utilization among patients with sickle cell disease.
Journal of health care for the poor and underserved